Stargardt’s Disease

ProQR childhood blindness drug succeeds in early study

Analysts, Blindness, Children, Clinical Trials, Cystic Fibrosis, Dystrophic Epidermolysis Bullosa, Gene Editing, Genetics, Leber’s Congenital Amaurosis 10, Mutations, R&D, RNA, Shares, Skin Disorders, Stargardt’s Disease, Usher Syndrome, Vision

An interim analysis of an early-stage trial showed that ProQR Therapeutics NV’s experimental treatment for a rare form of childhood blindness improved vision.

September 5, 2018/by Reuters Health