The U.S. Food and Drug Administration granted full approval to Orphalan’s Cuvrior (trientine tetrahydrochloride) for the treatment of Wilson’s disease, a rare genetic disorder. The approval announcement marks the first new treatment available for patients in over five decades.

Toronto-based biotech Deep Genomics landed $180 million in the company’s oversubscribed Series C.

Dr. Reddy’s Laboratories Ltd. announced the launch of Trientine Hydrochloride Capsules USP, 250 mg, a therapeutically equivalent generic version of Syprine (trientine hydrochloride) Capsules, approved by the U.S. Food and Drug Administration for treating Wilson’s disease.

Pfizer acquired a 15 percent stake in Vivet Therapeutics as well as an exclusive option to fully acquire the business, a deal that will give the New York-based pharma giant access to the French company’s experimental gene therapy for a rare genetic disorder.

Shares of beleaguered Dimension Therapeutics Inc. soared more than 160 percent in premarket trading after gene therapy company Regenxbio Inc. announced its acquisition via an all-stock deal.

NEW YORK – A New York Times article excoriated Valeant Pharmaceuticals International, Inc. (VRX) for the amount the company spends on research and development versus the amount it spends on mergers and acquisitions after the Quebec-based company quadrupled the price on a 55-year-old drug that treats Wilson Disease, a genetic disorder.   The Times highlights […]