https://www.pharmalive.com/wp-content/uploads/2020/01/Pharmalive_4c-300x37.png00BioSpacehttps://www.pharmalive.com/wp-content/uploads/2020/01/Pharmalive_4c-300x37.pngBioSpace2019-08-02 12:39:282019-08-02 13:03:30Amicus Therapeutics' Gene Therapy for Rare, Fatal Childhood Disease Shows Promise in Study