Following the ongoing trend in the pharmaceutical industry, bluebird bio orchestrated a restructuring that includes saving financially and cutting staff. The restructuring is designed to prolong the company’s budget as bluebird bio awaits decisions from the U.S. Food and Drug Administration (FDA).
bluebird bio Presents New Results from Clinical Development Program of eli-cel Gene Therapy for CALD
Biologics License Application (BLA), Cerebral Adrenoleukodystrophy (CALD), Clinical Trial Endpoints, Clinical Trials, Committee for Medicinal Products for Human Use (CHMP), Data, Efficacy, European Medicines Agency (EMA), Gene Therapy, Major Functional Disabilities (MFDs), Marketing Authorization Application (MAA), Neurological function, R&D, Rare Metabolic Disordersbluebird bio Inc. announced updated results from the clinical development program for the company’s investigational elivaldogene autotemcel (eli-cel, Lenti-D) gene therapy in patients with cerebral adrenoleukodystrophy (CALD), including long-term results from the Phase 2/3 Starbeam study and data from the Phase 3 ALD-104 study.