Platelet Count Archives

FDA approves CTI BioPharma’s bone marrow cancer drug

Analysts, Approvals, Bone Marrow Cancer, FDA, Forecasts, Incyte, Janus Kinase (JAK) Inhibitors, Myelofibrosis, Platelet Count, R&D, Therapeutics

The U.S. Food and Drug Administration approved CTI BioPharma Corp.’s drug for treating adult patients with a type of bone marrow cancer who also have low blood platelet count.

Solid Biosciences shares plummet as gene therapy trial halted again

Analysts, Bleeding, Clinical Hold, Duchenne Muscular Dystophy (DMD), Gene Therapy, Men, Muscle Wasting Disorders, Platelet Count, R&D, Red Blood Cell

Shares in Solid Biosciences Inc. plunged 71 percent after a clinical trial testing the company’s gene therapy for a muscle-wasting disorder was halted for the second time in less than two years.

EU panel approves drug for rare genetic disease

Blood, Committee for Medicinal Products for Human Use (CHMP), European Medicines Agency (EMA), Familial Chylomicronemia Syndrome (FCS), Fat Accumulation, FDA, FDA/Regulatory, Inflammation, Pancreas, Platelet Count, Rare Genetic Diseases, Recommended For Approval

An advisory committee of the EMA recommended conditionally approving a drug from Akcea Therapeutics and Ionis Pharmaceuticals that aims to treat a rare genetic disease.