Scientists at Stanford University School of Medicine have used the CRISPR gene-editing tool to repair the gene that causes sickle cell disease in stem cells.

Merck KGaA expects to continue delivering market-beating sales growth, helped in part by new gene modification techniques.

Startup Homology Medicines Launches With $43 Million Series A, To Be Led By Three Former Shire Execs   May 2, 2016By Mark Terry, BioSpace.com Breaking News Staff   Lexington, Mass.-based Homology Medicines launched today with a $43.5 million Series A preferred stock financing. The round was co-led by 5AM Ventures and ARCH Venture Partners. They […]

(Reuters) – A baby whom doctors thought almost certain to die has been cleared of a previously incurable leukemia in the first human use of an “off-the-shelf” cell therapy from Cellectis that creates designer immune cells. One-year-old Layla had run out of all other treatment options when doctors at Britain’s Great Ormond Street Hospital (GOSH) […]

As drugmakers including Novartis, Juno Therapeutics and Kite Pharma race to launch what may be the most effective treatments ever seen for leukemia and other blood cancers, they are grappling with how to make them widely available in a reliable and cost-efficient way.   The new therapies, known as CAR T cells, are made by […]