Novartis’ Promacta receives FDA breakthrough designation for new indication

 

Novartis drug Promacta has received breakthrough therapy designation from the U.S. Food and Drug Administration for first-line treatment of severe aplastic anemia (SAA).

The drug has received the designation for use in combination with standard immunosuppressive therapy in treating the rare blood disorder in which a patient’s bone marrow fails to produce enough red blood cells, white blood cells and platelets, the Swiss drug maker said on Thursday.

Promacta is already approved as a second-line therapy in SAA, as well as for adults and children with chronic immune thrombocytopenia.

Breakthrough status is a designation given to treatments demonstrating substantial improvement over existing therapies in treating a serious or life threatening illness.

Novartis said it expects regulatory filings in both the United States and the European Union this year.

 

(Reporting by Brenna Hughes Neghaiwi; Editing by Maria Sheahan)

 

Reuters source:

https://www.reuters.com/article/us-novartis-promacta/novartis-promacta-receives-fda-breakthrough-designation-for-new-indication-idUSKBN1ET0KL