Tag Archive for: DMD

The company was evaluating the efficacy and safety of pamrevlumab in a late-stage trial in patients with non-ambulatory Duchenne muscular dystrophy (DMD), where upper limb function of the patients are affected, versus a placebo.

Shares of Sarepta Therapeutics slumped as much as 21% on Friday over uncertainty on approval of its gene therapy for Duchenne muscular dystrophy after the U.S. health regulator reversed its decision on a panel meeting.