Research scientists from the School of Biomedical Engineering at the University of British Columbia have found that a colony-stimulating factor 1 receptor (CSF1R) inhibitor, best known as a cancer drug, may also be a potential treatment for Duchenne muscular dystrophy (DMD), a severe genetic disorder afflicting the muscles.
Tag Archive for: rare diaease
An interim analysis of AstraZeneca and partner Ionis Pharmaceuticals’ eplontersen showed the experimental drug met the main goals in a late-stage trial in patients with a rare, fatal disease, the Anglo-Swedish drugmaker said on Tuesday.
