Cranbury, N.J.-based Amicus Therapeutics and the Perelman School of Medicine at the University of Pennsylvania are expanding their gene therapy collaboration.
Expansion Therapeutics officially launched with the close of a $55.3 million Series A financing.
The U.S. FDA’s PCNSC voted against a recommendation for Sarepta Therapeutics’ eteplirsen for Duchenne Muscular Dystrophy (DMD).
STANFORD, Calif., July 12, 2015 /PRNewswire/ — Recent developments in stem cell research provide enormous potential for the field of regenerative medicine. Researchers are exploring how stem cell therapeutics might be able to treat and possibly even reverse the effects of many debilitative diseases including Alzheimer’s, type 1 diabetes and muscular dystrophy. Working professionals can now […]