MedAdNews spoke with Andrew Bast, chief strategy officer of Greater Than One, about the critical importance of health literacy for patients, brands, and marketers.
Tag Archive for: rare disease
The Genetic Metabolic Diseases Advisory Committee will meet on Friday to discuss Zevra’s modified scale to describe the efficacy of its drug candidate for the treatment of Niemann-Pick disease type C.
The drugmaker has cut jobs, bolstered its pipeline for rare disease medicines through takeover deals and unveiled new products, such as Alzheimer’s disease drug Leqembi, as part of a plan to return to growth.
AstraZeneca beat analyst expectations for its second-quarter revenue on strong demand for its cancer, rare disease and heart disease medicines.
Two-thirds of rare disease patients and caregivers from four countries report that the rare disease diagnosis took up to five years, while more than half of patient report being misdiagnosed at least once.
In a political climate where discourse is often marked by division, there remain crucial issues that bridge partisan divides. The vital importance of treating children living with rare diseases is certainly one such cause.
The U.S. health regulator has declined to approve Rocket Pharmaceuticals’ gene therapy to treat a rare and severe pediatric disorder that causes the immune system to malfunction.
Teva Pharmaceuticals sued rival drugmaker Corcept Therapeutics in federal court in San Francisco, accusing it of monopolizing the market for mifepristone-based Korlym, used to treat a rare hormonal disorder called Cushing’s syndrome.
To successfully launch rare disease drugs, with their small patient populations and high costs, pharma manufacturers need to get payers involved in discussions as soon as possible to ensure patient access.
Medicines for rare diseases are a leading contributor to all novel drug approvals and launches.